A recent review highlighted the importance of managing cardiovascular risk factors in patients with Fabry disease versus the general population.

(BPT) – Living with a rare disease may not be as rare as you would think: Affecting one in 10 Americans, there are more than 10,000 known rare diseases in the U.S. 1 While significant strides to ...

Philadelphia, PA - A two-year follow-up study of 25 patients with Fabry disease who received enzyme-replacement therapy (ERT) found that those with already-impaired kidney function had worse clinical ...

Sangamo Therapeutics, Inc. (SGMO) has been able to make several great advancements regarding its pipeline in the past year. The most notable program advancement would be regarding the fact that the ...

STAAR study demonstrated positive mean annualized estimated glomerular filtration rate (eGFR) slope at 52-weeks across all dosed patients in the study, which U.S. Food and Drug Administration (FDA) ...