The study provides evidence of survival benefits among patients with Duchenne muscular dystrophy (DMD) receiving eteplirsen compared with the natural history of the condition. DMD is a genetic ...
Sarepta Therapeutics said it will update its prescribing information for Elevidys ® (delandistrogene moxeparvovec-rokl) after acknowledging the sudden death of a patient with Duchenne muscular ...
The patient in this case had suffered acute liver failure following the Elevidys infusion. Sarepta Therapeutics announced that a patient with Duchenne muscular dystrophy (DMD) who received Elevidys ...
Even as investors punished Sarepta Therapeutics (NASDAQ: SRPT) after it disclosed the death of a patient treated with its Duchenne muscular dystrophy (DMD) gene therapy Elevidys ® (delandistrogene ...
Shares of Sarepta Therapeutics SRPT nosedived 42% in pre-market today after the company reported a second patient death following treatment with Elevidys, its one-shot gene therapy for Duchenne ...
Solid Biosciences (SLDB) is hoping to advance a next-generation gene therapy for the treatment of patients with Duchenne Muscular Dystrophy [DMD]. This would be with a gene therapy candidate by the ...
Following a review of safety data in the ambulatory DMD population, the FDA had recommended the removal of the voluntary hold for these patients. The Food and Drug Administration (FDA) is allowing ...
Consensus directed medical therapy (CDMT) was used in 73.1% of DMD patients with moderate or severe left ventricular dysfunction, leaving nearly 30% without recommended treatment. Target doses were ...
A recent study encapsulates how patients and caregivers characterize the impact of Duchenne muscular dystrophy (DMD) on patients’ physical limitations and symptom burden, potentially helping to inform ...
Satellos’ small-molecule therapy for Duchenne muscular dystrophy (DMD) has shown signals of improving grip strength in adult patients in a Phase I trial. The Phase Ib portion of the open-label study ...
Dentistry.com reports that rising dental emergencies are increasing demand for after-hours dentist services, alleviating ...
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