An experimental gene therapy seems to slow the progression of Huntington’s disease by about 75 per cent, and researchers are ...

This year saw notable progress in head and neck cancers, Huntington's disease, personalized genetic therapy, and heart ...

For decades, geneticists have known that most common illnesses are not caused by a single rogue gene but by intricate ...

X-linked retinoschisis gene replacement therapy, aiming to improve retinal architecture and visual function in young male ...

The baby saved from a rare disease by a first-ever personalized gene fix has reached a big milestone, taking his first steps ahead of Christmas. KJ Muldoon is walking and getting ready to celebrate ...

Genetic defects are exceedingly common, which is not surprising considering just how many cells make up our bodies, including our reproductive cells. While most of these defects have no or only minor ...

CRISPR is one of the most revolutionary technologies of the modern era, and now it's being used to bring back long-lost genes ...

At the Cleveland Clinic, doctors are using a one-time gene-editing therapy that alters a patient’s own blood-forming stem cells to correct the genetic mutation responsible for the disease. Physicians ...

A 10-month-old baby who sparked nationwide headlines after receiving a first-of-its kind gene-editing treatment was released ...

Don and Anne Edwards have donated $11 million to Ann & Robert H. Lurie Children's Hospital to establish what will be the ...