A new tablet formulation of SMA treatment Evrysdi (risdiplam) may give patients more "freedom and independence," a Genentech ...

Treatment with Spinraza (nusinersen) can help stabilize or improve motor function in adults with SMA, according to a new ...

A higher dose of Spinraza may be more effective than the currently approved dosing schedule for maintaining motor function in ...

Over 95% of babies now diagnosed with SMA are treated with Zolgensma gene therapy, per Daniel Grant, vice president for ...

Activating a protein called potassium channel Kv2.1 may help improve motor function in SMA, making it a potential SMA ...

In the last of a series, columnist Sherry Toh shares how she's coping with an intense leg of her journey with chronic pain ...

Activating a protein called potassium channel Kv2.1 may help improve motor function in SMA, making it a potential SMA ...

After facing several damaging storms, columnist Helen Baldwin was delighted to see a daffodil blooming amid the chaos.

Children with SMA given the gene therapy Zolgensma in infancy are maintaining motor milestones after up to 10 years, new ...

Columnist Sherry Toh thanks the dedicated nurses who've attended to her at various hospitals and at home over the years.

The SMA gene therapy candidate OAV101 IT, a version of Zolgensma, can be safely given to previously treated patients, per new ...