Gene therapies have the potential to cure some diseases, but they are extraordinarily expensive. Location can also be a big ...

Gene therapy has been successfully used to treat a number of diseases, including immune deficiencies, hereditary blindness, hemophilia and, recently, Huntington's disease, a fatal neurological ...

A massive genomics effort has identified thousands of single nucleotide non-coding variants, which alter gene activity, that link to disease and health.

Gene therapies have the potential to cure some diseases, but they are extraordinarily expensive. Location can also be a big ...

As Uganda rolls out mandatory nationwide screening of newborns for sickle cell disease this month, a gene therapy celebrated in the United States and Europe remains financially out of reach for most ...

Less than 2% of the genome codes for proteins; the rest, once called 'junk DNA', contains regulatory elements. Researchers ...

Children with certain genetic defects affecting hunger control can become severely obese from the age of one or two. Findings suggest that medicines based on GLP-1 hormone may work.

Since 2023, the club has built five libraries in local parks. In order to expand, volunteers and books are needed.

As CGRP-targeted therapies move into wider use, new data are beginning to clarify their role in special populations, the value of switching agents when one fails, and their long-term vascular safety.

PDUFA action date set for August 23, 2026If approved, DTX401 will be the first treatment to address the underlying cause of GDSIaNOVATO, Calif., ...

Oscar winner Gene Hackman, pianist wife Betsy Arakawa and one of their dogs were found dead in their Santa Fe home last ...