Kerala's Health Department extends free Risdiplam supply to Spinal Muscular Atrophy patients up to 25 years, broadening the previous limit of 12 years. This initiative under the CARE program, launched ...

In a major policy decision announced on Rare Disease Day, Kerala''s Health Department has extended free access to the high-cost drug Risdiplam for patients diagnosed with Spinal Muscular Atrophy (SMA) ...

Jesy Nelson broke down in tears after her campaign for more health checks on babies reached 100,000 signatures - meaning it ...

Young internet sensation Neilah, living with spinal muscular atrophy, has passed away. Her mother, Ruth Wambui, shares their ...

Gemma Biotherapeutics ("GEMMABio"), a clinical‑stage global genetic medicines company, announced today that the first patient has been dosed in the Phase 1/2 CHARISMA clinical trial of GB221, an ...

Discover how a 10-year-old boy with spinal muscular atrophy finds freedom and strength through swimming, inspiring others to defy physical limits. Read more at straitstimes.com. Read more at ...

The president's annual State of the Union address is tonight. Who are the guests coming with central Ohio's congressional ...

The Curious Case Of… examines Sarah Delashmit’s decades-long medical fraud, from faking muscular dystrophy and cancer to her federal conviction and prison sentence for wire and mail fraud.

Pinnock tells PEOPLE all three remaining Little Mix members reconnected with Jesy Nelson after she announced her daughters' spinal muscular atrophy diagnosis ...

Experts call for early diagnosis, prophylaxis in hemophilia, improved MS policy frameworks, genomic testing access and ...

Fast functional testing of genetic variants, from newborn genomes to disease models like zebrafish, is transforming ambiguous DNA findings into confident, real‑time treatment decisions.