Today there are injected medicines that block proteins produced by the PCSK9 and ANGPTL3 genes in the liver, thus helping the body clear away cholesterol. The new research uses CRISPR, the Nobel Prize ...

By Hugo Francisco de Souza Emerging research suggests reversible RNA editing mechanisms may influence heart disease biology while opening new avenues for biomarkers and next-generation cardiovascular ...

Researchers have found that a new base-editing gene therapy can help treat a rare neurodevelopmental disorder called Snijders Blok–Campeau syndrome caused by mutations in the CHD3 gene. A specialized ...

Scientists are testing an entirely new way to fight heart disease: a gene-editing treatment that might offer a one-time ...

Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic ...

The research team, led by scientists including Ryo Hashizume, worked with skin cells and induced pluripotent stem cells derived from people with Down syndrome. Rather than altering individual genes, ...

UCLA researchers have developed a lipid nanoparticle-based gene-editing approach capable of inserting an entire healthy gene ...

Mayo Clinic researchers have developed a promising gene-editing therapy that directly corrects a genetic mutation responsible for autosomal dominant polycystic kidney disease (ADPKD), the most common ...

SAN DIEGO - Bionano Genomics, Inc. (NASDAQ:BNGO) announced Wednesday that a peer-reviewed study has demonstrated the effectiveness of optical genome mapping (OGM) in detecting genomic alterations ...

FDA Commissioner Marty Makary says the agency wants to remove barriers for patients suffering from rare genetic conditions.

Gene editing has enormous potential to help feed the world’s growing population, but it’s currently difficult, time-consuming ...