StitchR makes it possible to deliver larger payloads with current vectors, expanding the list of diseases targetable by gene therapies.

StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models.

Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is a big problem: size.

The Keeneland November Breeding Stock Sale concluded its nine-day run in Lexington Wednesday with vibrant trade from a diverse buying bench leading to across-the-board increases where were highlighted ...

A total of 105 head sold for $8,620,500, with an average of $81,325 and a median of $47,500. The median and average were up ...

To determine the type and severity of a cancer, pathologists typically analyze thin slices of a tumor biopsy under a ...

The researchers found cordycepin triphosphate blocks two separate signaling pathways often hijacked by cancer cells to assist ...

Kebilidi is the first approved gene therapy that can be directly administered to the brain. Its OK secures a priority review ...

Harvard researchers pioneered a method called HACE for targeted gene mutations, advancing genetic research potential.

Becomes first company to showcase four routes of synthesis for approved siRNA therapeutic asset——Joint poster with Bachem demonstrates ...

New research has identified distinct neural circuits for the anti-anxiety and hallucinogenic effects of psychedelics.

Next-generation metagenomic sequencing test developed at UCSF proves its effectiveness in quickly diagnosing almost any kind ...