A young man with Duchenne MD and treated with Elevidys has died of acute liver failure, Sarepta reports; it's working with ...

Columnist Betty Vertin says her youngest daughter is starting to become aware of her older brothers' health challenges with DMD.

Columnist Shalom Lim is sad to say goodbye to his caregiver of 18 years, but looks forward to the new chapter of life this ...

A comprehensive care approach can help people with ambulatory DMD maximize function and retain the ability to walk for as ...

RGX-202, a DMD gene therapy, has been well tolerated in an ongoing clinical trial and improved motor function for DMD boys, per interim data.

AskBio has dosed the first participant in the second group of a Phase 1/2 trial of AB-1003, an experimental gene therapy for ...

An onslaught of new setbacks due to FSHD disease progression has left columnist Robin Stemple understandably anxious about ...

Columnist Patrick Moeschen offers a retrospective of what he did and didn't know about living with muscular dystrophy over ...

Columnist Betty Vertin has a day of heightened awareness about her sons' experience with wheelchairs and life with DMD.

Capricor Therapeutics’ investigational therapy deramiocel, formerly CAP-1002, which is being considered for approval in the U.S., continued to show an ability to preserve upper limb function in boys ...