The specialty pharmacy Orsini was selected as a partner to provide Itvisma, the newly approved gene therapy for people with ...

Columnist Sherry Toh prefers holiday giving rather than receiving and making others happy, because what she wants isn't found in stores.

Columnist Connie Chandler gives thanks for the acts of kindness her caregivers perform — the sweet stuff that makes life so ...

The U.S. Food and Drug Administration has approved Itvisma as the first gene therapy for spinal muscular atrophy patients ...

A high-dose regimen of nusinersen (Spinraza) has been recommended for approval by the CHMP, marking a potential new option ...

Guest writer Kelly Bertsch initially felt hopeless after her son Luke's SMA diagnosis, but she is now watching his bright ...

During this season of Thanksgiving, columnist Halsey Blocher reminds readers that they don't have to give a lot to make an impact.

Columnist Sherry Toh reflects on winning her second achievement award this year and thanks all those who supported her along ...

Kelly Bertsch is the mother of Luke Bertsch, 15, who lives with spinal muscular atrophy type 2. Luke was diagnosed just ...

When columnist Ari Anderson moved upstairs for a few days, it required a lot of logistical planning. Seemingly small changes ...

SMA expert Brian Lin, PhD, shares his thoughts on aging with SMA, treatment, advocacy, and supporting patients across their ...