Columnist Robin Stemple struggles to feel grateful on difficult days with FSHD, but still tries to recognize his many ...

The FDA updated prescribing information for Elevidys with new safety warnings and limiting its use to DMD patients who can ...

New research shows DMD is marked by abnormalities in muscle development in the womb, supporting the potential of a therapy ...

With three sons with Duchenne MD, columnist Betty Vertin has little time for housework, making her regret not giving the other kids chores.

Columnist Shalom Lim reflects with gratitude on how he's found purpose by supporting other Singaporeans on their own health ...

Columnist Betty Vertin's track career ended years ago, but she never stopped lifting weights — only now its the emotional weight of Duchenne.

A Phase 1/2 clinical trial testing SRP-1003 for myotonic dystrophy type 1 is progressing with higher doses as planned.

When in the course of human events, it becomes necessary to make choices, we must first consider our options. Congratulations! By reading these words, you have made a choice to crawl into my brain ...

When I was a young mom watching my oldest daughter, Lexi, move from upper elementary to middle school, I often felt heartbroken and helpless. She was an excellent student and friend at school, but ...

Histone deacetylase inhibitors are a treatment approach designed to work by blocking an enzyme that turns off gene activity. This may ultimately help by slowing muscle loss and disease progression.

A young man with Duchenne muscular dystrophy (DMD) who received the one-time gene therapy Elevidys (delandistrogene moxeparvovec-rokl) has died due to acute liver failure. In a statement, the ...